autores Patrícia Espinheira de Sá Maciel Da Silva JD Andreia Teixeira-Castro Castro, Andreia Cristiana Teixeira MacIel, P.
palavras-chave Animals Ataxin-3 Genetic Therapy Humans Machado-Joseph Disease Molecular pathogenesis Neurodegeneration Protein Biosynthesis Repressor Proteins Spinocerebellar ataxia type 3 Therapeutic advances