autores Patrícia Espinheira de Sá Maciel Da Silva JD Da Silva, JD. Andreia Teixeira-Castro Castro, Andreia Cristiana Teixeira MacIel, P.
palavras-chave Animals Ataxin-3 Genetic Therapy Humans Machado-Joseph Disease Molecular pathogenesis Neurodegeneration Protein Biosynthesis Repressor Proteins Spinocerebellar ataxia type 3 Therapeutic advances
Digital Object Identifier (DOI) https://doi.org/10.1007/s13311-019-00798-1 https://doi.org/10.1007/s13311-019-00798-1